Travis Smith was a very serious baby. Born completely unable to hear, his mother Sierra struggled to see his personality shine through his mute world. | Travis Smith was a very serious baby. Born completely unable to hear,

Cell and gene therapies are moving towards correcting root causes of diseases. Let's take a look at future cell and gene therapy trends.

Gene therapy represents one of medicine’s most ambitious attempts to treat disease at its root cause by altering the genetic code itself. The approach works by recovering the functions of critical proteins that serve as the workhorses of cells and form ...

The Breakthrough Prize Foundation awarded researchers involved in developing gene therapies for blindness and sickle cell disease.

Three Philadelphia scientists won a $3 million Breakthrough Prize for developing the first FDA-approved gene therapy for a genetic disease, prize sponsors announced Saturday. Their work created a scientific and regulatory road map for gene therapies,

The FDA’s recently unveiled plausible mechanism framework may have been forged with i | The FDA’s newly launched plausible mechanism framework may have been forged in the image of individualized therapies,

We are delighted by the Breakthrough award, but we accept it representing this brilliant team of people at Penn,” Bennett said. “Yeah, it’s really a Penn achievement.”

The skin over a fresh wound might not look like much. In some animals, though, that thin covering becomes command central for rebuilding what was lost.

To Ocugen CEO Shankar Musunuri, Ph.D., most gene therapy biotechs today lack vision. | Many gene therapy outfits focus on technical advances, Ocugen CEO Shankar Musunuri, Ph.D., said, meaning they miss out on broader commercial success.